At Risk for Huntington's Disease

HD is a genetically caused brain disorder that causes uncontrollable bodily movements and robs people's ability to walk, talk, eat, and think. The final result is a slow, ugly death. Children of parents with HD have a 50-50 chance of inheriting the disease. There is no cure or treatment.

Showing posts with label Enroll-HD. Show all posts
Showing posts with label Enroll-HD. Show all posts
Thursday, June 18, 2026

With the ‘worst’ FDA head out and Huntington’s disease advocates pressing for bipartisan reform, uniQure announces new plan to seek gene therapy approval

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   On June 17, uniQure announced a new plan to apply to the U.S. Food and Drug Administration (FDA) to seek approval of its ge...
Wednesday, April 22, 2026

As FDA faces demands for greater clarity, uniQure presses ahead in search for Huntington’s disease gene therapy approval

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   As the reportedly dysfunctional U.S. Food and Drug Administration (FDA) faces demands for greater clarity in the wake of r...
Monday, March 09, 2026

CHDI chief scientist: ‘at the precipice’ of treatments, Huntington’s disease community must ‘persevere’ through the stress

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   As researchers have hypothesized that lowering (reducing) the amount of abnormal huntingtin protein in the brains of people...
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