At Risk for Huntington's Disease

HD is a genetically caused brain disorder that causes uncontrollable bodily movements and robs people's ability to walk, talk, eat, and think. The final result is a slow, ugly death. Children of parents with HD have a 50-50 chance of inheriting the disease. There is no cure or treatment.

Showing posts with label Robert Pacifici. Show all posts
Showing posts with label Robert Pacifici. Show all posts
Monday, March 09, 2026

CHDI chief scientist: ‘at the precipice’ of treatments, Huntington’s disease community must ‘persevere’ through the stress

›
   As researchers have hypothesized that lowering (reducing) the amount of abnormal huntingtin protein in the brains of people...
Monday, March 02, 2026

FDA recommends a full clinical trial for uniQure Huntington’s disease drug, further delaying potential approval

›
   Delaying but not blocking AMT-130, uniQure’s  emerging gene therapy to slow Huntington’s disease progression, the U.S. Food...
Monday, February 23, 2026

uniQure’s AMT-130 at the forefront of 21st Huntington’s Disease Therapeutics Conference

›
   AMT-130, the uniQure  gene therapy that successfully slowed the progression of Huntington’s disease  before being obstruct...
›
Home
View web version

About Me

Gene Veritas
View my complete profile
Powered by Blogger.