At Risk for Huntington's Disease

HD is a genetically caused brain disorder that causes uncontrollable bodily movements and robs people's ability to walk, talk, eat, and think. The final result is a slow, ugly death. Children of parents with HD have a 50-50 chance of inheriting the disease. There is no cure or treatment.

Showing posts with label clinical trials. Show all posts
Showing posts with label clinical trials. Show all posts
Sunday, July 12, 2026

Citing lack of efficacy, Roche halts two Huntington’s disease drug programs, while other initiatives forge ahead

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   In deeply disappointing news for the Huntington’s disease community and beyond, Roche  announced on July 9 that it stopped ...
Thursday, June 18, 2026

With the ‘worst’ FDA head out and Huntington’s disease advocates pressing for bipartisan reform, uniQure announces new plan to seek gene therapy approval

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   On June 17, uniQure announced a new plan to apply to the U.S. Food and Drug Administration (FDA) to seek approval of its ge...
Sunday, April 05, 2026

A Senate probe of the FDA and a letter from advocates to Trump could aid in approval of Huntington’s disease gene therapy

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   Two key political developments could aid uniQure’s  effort to seek approval of its historically efficacious Huntington’s d...
Monday, March 02, 2026

FDA recommends a full clinical trial for uniQure Huntington’s disease drug, further delaying potential approval

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   Delaying but not blocking AMT-130, uniQure’s  emerging gene therapy to slow Huntington’s disease progression, the U.S. Food...
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